Living with DM1 has profound impacts on every part of people’s lives, including work, social interactions and family relationships. Community members have shared their moving perspectives of living with DM1 with our team, including what it would mean to them to have a potentially transformative therapeutic for their disease. These insights are guiding our efforts to develop therapies that deliver meaningful functional improvement for people living with DM1.
DM1 Stories
Each person living with DM1 has
a unique and powerful story to tell
a unique and powerful story to tell
On September 7, we join the Duchenne community for World Duchenne Awareness Day, making a difference by focusing on therapies that are designed to deliver functional improvement for individuals living with DMD.
Meet Sarah
Sarah shares the impact DM1 has on her and her family and why a potentially transformative therapy is urgently needed
Meet BillyDean and Suzette
Through their resilience and Suzette’s incredible advocacy efforts for her son, BillyDean, they succeeded in getting a DM1 diagnosis and have been learning how to live and thrive ever since
Meet Loraine
A courageous family battle and devotion in the face of generational adversity
